We take pride
in our mission - to discover, develop and deliver a broad portfolio of transformative therapies for patients with genetic diseases around the world. We are building an industry-leading, end-to-end gene therapy powerhouse to create a better future for patients living with rare and underserved diseases.
A leading pipeline
We are developing one of the world's most robust pipelines of gene therapies for genetic disorders.
Our Commitment to Patients and Families
At Astellas Gene Therapies, we believe our strong relationships with patients and families help us to better understand the diseases we target and optimize our research, clinical development and commercial plans. Our goal is to deliver meaningful gene therapy clinical development programs, educational materials, and resources to benefit patients with limited or no treatment options, including rare diseases and cancer.